The Metreleptin Effectiveness and Safety Registry (MEASuRE): concept, design and challenges

  1. Haymond, M.W.
  2. Araújo-Vilar, D.
  3. Balser, J.
  4. Lewis, J.H.
  5. Louzado, R.
  6. Musso, C.
  7. von Schnurbein, J.
  8. Wabitsch, M.
Revista:
Orphanet Journal of Rare Diseases

ISSN: 1750-1172

Ano de publicación: 2023

Volume: 18

Número: 1

Tipo: Artigo

DOI: 10.1186/S13023-023-02714-5 GOOGLE SCHOLAR lock_openAcceso aberto editor