Elosulfase alfa for mucopolysaccharidosis type IVA: Real-world experience in 7 patients from the Spanish Morquio-A early access program

  1. Pintos-Morell, G.
  2. Blasco-Alonso, J.
  3. Couce, M.L.
  4. Gutiérrez-Solana, L.G.
  5. Guillén-Navarro, E.
  6. O'Callaghan, M.
  7. del Toro, M.
Journal:
Molecular Genetics and Metabolism Reports

ISSN: 2214-4269

Year of publication: 2018

Volume: 15

Pages: 116-120

Type: Article

DOI: 10.1016/J.YMGMR.2018.03.009 GOOGLE SCHOLAR lock_openOpen access editor
Data source: Scopus